Eli Lilly and Regeneron are leading the push to treat congenital deafness with gene therapies, seeking a piece of a potential ...
Gene therapy represents one of medicine’s most ambitious attempts to treat disease at its root cause by altering the genetic code itself. The approach works by recovering the functions of critical ...
Five-year clinical study results show this revolutionary one-time treatment allowed 94% of patients to stop routine factor IX prophylaxis DETROIT, March 23, 2026 /PRNewswire/ -- The Barbara Ann ...
An expert involved in the first successful gene therapy trial for Huntington's Disease discusses the trial results and ...
With promise to slow aging and cure some types of cancer, a new gene therapy presents cost and access hurdles for CT patients ...
The last available hemophilia gene therapy is temporarily unavailable, according to CSL Behring.  | The company is working ...
The Greater Philadelphia Business Coalition on Health webinar series provided an in-depth framework for the advantages of including cell and gene therapy coverage in employer health plans, as well as ...
A genetic variant carried by at least one-fifth of the population may do far more than raise the odds of developing Alzheimer ...
A new method for safely inserting large chunks of DNA into genomes has now measured up in mice, potentially paving the way ...
Chantez Sanford Jr., 24, of Southfield, says his life has been transformed after undergoing Lyfgenia gene therapy at Children ...
She has a genetic condition that affects motor nerve cells in the spinal cord, causing progressive muscle weakness. Read more ...
After telegraphing an investigation in November, the FDA has moved to restrict the use of bluebird bio’s gene therapy Skysona in certain patients. The FDA has updated Skysona’s indication, allowing it ...